Switching off one copy of a gene also enabled one of the children to walk independently for the first time.
24 July 2026
Switching off one copy of a gene also enabled one of the children to walk independently for the first time.
Targeting neurons (artist’s illustration) that had an abnormal flow of sodium ions reduced epileptic seizures in two people. Credit: Kateryna Kon/SPL
A tailored treatment has reduced seizures and improved developmental skills in two boys with debilitating neurological disorders1.
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