Encoded Therapeutics gives a heads-up to other gene therapy company about the trade-offs with a drug meant to improve safety.
Camille MacMillan/STAT
By Jason Mast
May 13, 2026
General Assignment Reporter
Jason Mast
Some in the gene therapy field lament lost time while Capsida kept silent about the brain receptor it was targeting when things…
A gene therapy that instructs cells to produce more of an anti-ageing protein called klotho is about to be offered by a US…
Regenxbio plans to submit its Duchenne gene therapy for FDA approval, just a month after it said that regulators wanted to see…
The FDA will reconsider approving Regenxbio's experimental gene therapy for a deadly and rare childhood brain disorder it…
Though two serious side effects muddied the results, CEO Curran Simpson expressed optimism about a clearance and claimed FDA…
The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy…
