Some in the gene therapy field lament lost time while Capsida kept silent about the brain receptor it was targeting when things went wrong.
Photo illustration: STAT; Photo: Adobe
By Jason Mast
May 12, 2026
General Assignment Reporter
Jason Mast
Encoded Therapeutics gives a heads-up to other gene therapy company about the trade-offs with a drug meant to improve safety.
The FDA will reconsider approving Regenxbio's experimental gene therapy for a deadly and rare childhood brain disorder it…
Death of youngster following experimental gene therapy only made public after journalists investigated
Scientist says child’s death reveals ‘serious failures in risk assessment, transparency and institutional oversight’.
With a second delayed report of a child's death in China, criticism is rising of a looser form of clinical trial. One expert:…
"A cutting-edge gene-editing trial in China went disastrously wrong. A family wants accountability."
