Ultragenyx shares rise after FDA approval of Genglycos, with a $2.7 million wholesale cost and $362 million peak sales estimate.

If at first you don’t succeed in gene therapy, then try, try again. | If at first you don’t succeed in gene therapy, then try, try again, is the lesson Ultragenyx likely took home…

FDA grants Ultragenyx's Genglycos accelerated approval, its first gene therapy, for GSDIa in patients 8 and up; list price $2.7M.