Gene therapy for Usher syndrome ‘encouraging’ in phase 1/2 trial

DENVER — A gene therapy showed “encouraging visual function improvements” in patients with Usher syndrome type 1B, according to a phase 1/2 trial presented at the Association for Research in Vision and Ophthalmology meeting. “Usher 1 syndrome is a disease in which children are born profoundly deaf,” Jayashree Sahni, MD, FRCOphth, PhD, EMBA, told Healio. “Over their lifetime, they start developing

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