The CHMP issues a negative opinion on Zevra Therapeutics' arimoclomol for Niemann-Pick disease type C, prompting a re-examination request.

Minoryx's leriglitazone (Nezglyal) won EU backing after two prior rejections, while CHMP rejected Zevra's arimoclomol (Meplyffa).

The CHMP issues a negative opinion on Zevra Therapeutics' arimoclomol for Niemann-Pick disease type C, prompting a re-examination request.