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Precision DNA editing targets root cause of severe childhood epilepsy in preclinical study

Gene editing can repair a DNA error in mice that causes Dravet syndrome, a rare, incurable, and potentially deadly form of childhood epilepsy. After the edit, the mice have far fewer seizures and live much longer.

Raccontata daeurekalert.org

Timeline cronologica

  1. domenica 17 maggio 2026·eurekalert.org

    Precision DNA editing targets root cause of severe childhood epilepsy in preclinical study

    Gene editing can repair a DNA error in mice that causes Dravet syndrome, a rare, incurable, and potentially deadly form of childhood epilepsy. After the edit, the mice have far…