It will change regulators’ rule books
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Our podcast on science and technology. Millions of children suffer from rare, often fatal diseases. A new class of customised…
Restrictions would do more harm than good
Regulators are now mulling the results of the late-stage trial
Blood filtering has performed well in early trials
The already fraught oversight of rare-disease treatments is becoming politicised
Widespread bans don’t seem to be a hindrance
